$4.25 million gene therapy for kids becomes world's priciest drug

$4.25 million gene therapy for kids becomes world's priciest drug 
NBC LEX18, by Alex Arger; 3/20/24 
A lifesaving gene therapy for children born with a rare and debilitating disease has just been approved by the U.S. Food and Drug Administration. The catch? Its wholesale cost has been set at $4.25 million, making it the most expensive medicine in the world. Orchard Therapeutics announced the hefty price for Lenmeldy Wednesday, two days after the FDA approved the therapy as the only treatment for kids with metachromatic leukodystrophy, or MLD.